Tag Archives: Rare

Albireo’s rare liver disease drug Bylvay scores back-to-back approvals in U.S., Europe

With a pair of approvals on both sides of the Atlantic, liver disease-focused biotech Albireo is off and running with its new medicine Bylvay. The oral drug, the first treatment for pruritus in patients with progressive familial intrahepatic cholestasis (PFIC), scored an FDA nod Tuesday and a European approval Monday. With the FDA’s blessing, Albireo is kicking off an “immediate”… Read More »

Innovative Imaging Technology Effectively Measures Disease Severity in Rare Neurodegenerative Disorder

A rapid, non-invasive eye exam that uses innovative imaging technology effectively measures the severity of disease in patients with a rare neurodegenerative disease called Friedrich ataxia, according to a study by Weill Cornell Medicine, Weill Cornell Medicine-Qatar and NewYork-Presbyterian researchers. The results suggest that the exam, known as corneal confocal microscopy (CCM), could be a… Read More »

I've Dealt With a Rare Skin Disorder All of My Life—Here's What It Taught Me About Beauty

When I was younger, I had a fear of makeup counters. The bright lights above the glass counters that made me feel more exposed, the intimidating line of products that promised to make me more beautiful, the judgment I felt as the makeup ladies approached me. Advertisement – Continue Reading Below See, while other kids… Read More »